Base editing rescue of spinal muscular atrophy in cells and in mice
Investigators
Arthur Burghes, Professor
Mandana Arbab
Zaneta Matuszek
Ailing Du
Gregory A Newby
Aditya Raguram
Michelle F Richter
Kevin T Zhao
Jonathan M Levy
Max W Shen
W David Arnold
Dan Wang
Jun Xie
Guangping Gao
Daivd R Liu
Filters: 2023